RECRUITING
NCT07286565
Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or Spinal Muscular Atrophy Identified by Newborn Screening
Updated: Dec 16, 2025
- RECRUITINGNCT07265232
Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle Income Countries (LMIC).
Updated: Dec 4, 2025 - RECRUITINGNCT07254988
Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders
Updated: Nov 28, 2025 - RECRUITINGNCT07231549
CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain
Updated: Nov 17, 2025 - RECRUITINGNCT07223489
Evaluate the Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in the MedStar Health System
Updated: Oct 31, 2025 - RECRUITINGNCT07223320
HABIT-ILE + FST in Children With SMA
Updated: Oct 31, 2025 - RECRUITINGNCT07190300
TulmiSTAR-02: A Phase I/II Open-label Study of Tulmimetostat in Combination With Darolutamide vs. Darolutamide, and Tulmimetostat With Abiraterone in Patients With Metastatic Hormone-sensitive Prostate Cancer (mHSPC)
Updated: Dec 2, 2025 - RECRUITINGNCT07047144
A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
Updated: Nov 19, 2025 - RECRUITINGNCT06978985
Adult SMA Research and Clinical Hub
Updated: May 18, 2025 - RECRUITINGNCT06977269
Safety and Tolerability of Low Motoneuron Stimulation Via Transcranial Magnetic Stimulation in Spinal Muscular Atrophy
Updated: Jun 18, 2025 - RECRUITINGNCT06971094
Safety and Efficacy Evaluation of GC101 Gene Therapy Via Intrathecal (IT) Injectionin the Treatment of Patients With Type 2 Spinal Muscular Atrophy (SMA) - Phase III
Updated: Jun 5, 2025 - RECRUITINGNCT06955897
Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA
Updated: May 2, 2025 - RECRUITINGNCT06862596
Clinical Trial of Mexiletine Hydrochloride for Spinal and Bulbar Muscular Atrophy
Updated: Apr 16, 2025 - RECRUITINGNCT06839469
Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders
Updated: Feb 21, 2025 - RECRUITINGNCT06764485
A Study to Compare the Efficacy and Safety of BMS-986365 Versus the Investigator's Choice of Therapy in Participants With Metastatic Castration-resistant Prostate Cancer
Updated: Dec 2, 2025 - RECRUITINGNCT06756633
Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular Diseases
Updated: Jan 3, 2025 - RECRUITINGNCT06666816
Observational Study to Observe Variations of Gait Parameters in Patients with Neuromuscular Diseases
Updated: Oct 31, 2024 - RECRUITINGNCT06648486
Robot-assisted Training
Updated: Aug 29, 2025 - RECRUITINGNCT06562283
Evaluation of the Reproducibility of a Fatigability Test Fitted to Patients With Spinal Muscular Atrophy
Updated: Dec 19, 2024 - RECRUITINGNCT06555419
A Study to Find Out How Nusinersen is Processed in the Body When Given Through the ThecaFlex DRx™ System in Adult and Pediatric Participants With Spinal Muscular Atrophy (PIERRE-PK)
Updated: Sep 8, 2025
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